The main problem is that most vector production technologies were developed for the lab, rather than to support industrial ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

AAV is a useful vector for delivering genes; however, the size of the gene that can be carried is limited. Therefore, Dr. Kamiya and his team constructed a base editing tool (SaCas9-NNG-ABE8e ...

The Viral Vector & Plasmid DNA Manufacturing Market Size accounted for USD 5.4 Billion in 2023 and is estimated to achieve a ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...

A recent study led by the Universitat Autònoma de Barcelona (UAB) demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, Megalencephalic Leukoencephalopathy ...

LUXTURNA uses an adeno-associated viral type 2 (AAV2) vector to deliver the RPE65 gene. The vector includes a cytomegalovirus (CMV) enhancer and a chicken beta-actin promoter to drive the ...